TREAT-NMD news Archives - TREAT-NMD Advancing diagnosis, care and treatment for people with neuromuscular diseases around the world Thu, 31 Jul 2025 15:43:59 +0000 en-GB hourly 1 https://www.treat-nmd.org/wp-content/uploads/2022/11/cropped-treat-favicon-32x32.png TREAT-NMD news Archives - TREAT-NMD 32 32 The Online Registry Portal Launch https://www.treat-nmd.org/the-online-registry-portal-launch/ Thu, 31 Jul 2025 15:42:45 +0000 https://www.treat-nmd.org/?p=9066 We’re excited to announce the phased launch of the new online communication portal designed specifically for registry network curators. As previewed during the June subgroup meetings, the Registry Portal is now being […]

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]]> The TREAT-NMD Advisory Committee for Therapeutics (TACT) https://www.treat-nmd.org/the-treat-nmd-advisory-committee-for-therapeutics-tact/ Thu, 31 Jul 2025 15:01:52 +0000 https://www.treat-nmd.org/?p=9058 The TREAT-NMD Advisory Committee for Therapeutics (TACT) is a globally recognised, multidisciplinary panel of experts that convenes several times a year to review and provide independent guidance on key aspects […]

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]]> Last Chance Early Bird Tickets for the TREAT-NMD International Conference – Lisbon, February 2026 https://www.treat-nmd.org/last-chance-early-bird-tickets-for-the-treat-nmd-international-conference-lisbon-february-2026/ Fri, 27 Jun 2025 16:44:58 +0000 https://www.treat-nmd.org/?p=8932 As the neuromuscular field continues to evolve, so do the challenges we face – whether it’s ensuring equitable access to therapies, navigating regulatory uncertainty, or aligning with the expectations of […]

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]]> Harnessing Technology to Improve Lives in Neuromuscular Disease https://www.treat-nmd.org/harnessing-technology-to-improve-lives-in-neuromuscular-disease/ Fri, 27 Jun 2025 12:30:56 +0000 https://www.treat-nmd.org/?p=8929 TREAT-NMD is taking bold steps to ensure it remains at the forefront of innovation in rare disease care. As a global leader in advancing treatments for neuromuscular disease through education, […]

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]]> Upcoming TREAT-NMD SMA and DMD Expert Masterclasses, Prague https://www.treat-nmd.org/upcoming-treat-nmd-sma-and-dmd-expert-masterclasses-prague/ Fri, 27 Jun 2025 11:54:36 +0000 https://www.treat-nmd.org/?p=8927   We are very pleased to be hosting another in our series of educational masterclasses in Prague next week. Across three days, we will run masterclasses aimed at healthcare professionals […]

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]]> Last chance to express your interest to attend the Duchenne Muscular Dystrophy Early Diagnosis Masterclass, hosted by TREAT-NMD and Parent Project Muscular Dystrophy (PPMD)! https://www.treat-nmd.org/express-your-interest-to-attend-the-duchenne-muscular-dystrophy-early-diagnosis-masterclass-hosted-by-treat-nmd-and-parent-project-muscular-dystrophy-ppmd/ Mon, 16 Jun 2025 09:19:42 +0000 https://www.treat-nmd.org/?p=8905 If you are a healthcare professional involved in the diagnosis of patients living with Duchenne muscular dystrophy (DMD), we invite you to express your interest in attending a virtual masterclass. The […]

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]]> Duchenne Muscular Dystrophy Early Diagnosis Project https://www.treat-nmd.org/duchenne-muscular-dystrophy-early-diagnosis-project/ Mon, 02 Jun 2025 13:50:18 +0000 https://www.treat-nmd.org/?p=8890 The increasing prevalence of newborn genetic screening has led to earlier DMD diagnoses, with more and more patients being diagnosed prior to the development of symptoms. However, minimal clinical guidance […]

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]]> New AAN Evidence in Focus Article Highlights Gene Therapy for Duchenne Muscular Dystrophy https://www.treat-nmd.org/new-aan-evidence-in-focus-article-highlights-gene-therapy-for-duchenne-muscular-dystrophy/ Thu, 29 May 2025 14:11:20 +0000 https://www.treat-nmd.org/?p=8876 The post New AAN Evidence in Focus Article Highlights Gene Therapy for Duchenne Muscular Dystrophy appeared first on TREAT-NMD.

]]> TREAT-NMD Announces Dr. Kathryn R. Wagner as New Chair of the Board https://www.treat-nmd.org/treat-nmd-announces-dr-kathryn-r-wagner-as-new-chair-of-the-board/ Wed, 28 May 2025 08:37:07 +0000 https://www.treat-nmd.org/?p=8866 20 May 2025 – TREAT-NMD, a global network dedicated to accelerating treatments for neuromuscular diseases, is pleased to announce the appointment of Kathryn R. Wagner, MD, PhD, as its new […]

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]]> Project PaLaDIn https://www.treat-nmd.org/project-paladin/ Tue, 27 May 2025 16:45:55 +0000 https://www.treat-nmd.org/?p=8860 TREAT-NMD is the scientific coordinator of the IHI funded project PaLaDIn. The PaLaDIn consortium includes partners from SMEs, academia and patient advocacy organisations, working together to develop and implement a […]

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