Reflecting on 15 Years of Progress: Highlights from the TACT Symposium Developing Therapies for Rare Neuromuscular Diseases
The recent TACT Symposium, Developing Therapies in Rare Neuromuscular Diseases, which took place in Boston on the 31st of October, highlighted significant progress made in developing therapies over the past 15 years. Bringing together experts, researchers, clinicians, and stakeholders, the symposium focused on key milestones and lessons learned in improving patient outcomes.
Key topics included the importance of preclinical research, patient perspectives, and robust, patient-centric outcome measures in shaping clinical trials. The discussions emphasised continued collaboration between researchers, healthcare providers, regulatory bodies, and patient communities to overcome challenges and advance treatment options.
While celebrating past achievements, the symposium also reminded us that the work to improve therapies for rare neuromuscular diseases continues, and TACT remains committed to making further progress.
Building Connections: TACT Symposium Networking Event
While in Boston, the TREAT-NMD team also hosted a Networking Event, offering a relaxed space for attendees to connect and share insights. Researchers, clinicians, patient advocates, and industry leaders engaged in meaningful discussions, fostering new collaborations essential for advancing rare disease therapies.
We are grateful to all participants and look forward to building on these connections to drive future progress in the development of therapies that will benefit patients worldwide.
