At TREAT-NMD, our commitment to advancing the diagnosis, treatment, and care for those affected by neuromuscular diseases is unwavering. We are thrilled to unveil our 2022 – 2023 impact report, showcasing the strides we’ve made in pursuit of this critical mission.
1. Informing the Community
A cornerstone of our work is keeping the neuromuscular disease community informed. Through our expansive network of experts, we provide updates on research, clinical trials, and best practices in care. This ensures that our community is empowered with the latest knowledge to navigate their journey with greater understanding and hope.
2. Connecting Stakeholders
Collaboration is at the heart of what we do. TREAT-NMD acts as a catalyst, working with key opinion leaders, patient organisations, and industry partners within the neuromuscular community. By fostering this interconnectedness, we promote knowledge-sharing and innovation, laying the groundwork for transformative advancements in therapies and treatments.
3. Advancing Therapeutics
Our dedication to advancing future trials and therapies is exemplified by our Advisory Committee for Therapeutics. Through collaborative efforts and expert insights, we accelerate the development of ground-breaking treatments and de-risk clinical trials, bringing us closer to effective interventions for neuromuscular diseases.
Key Highlights from the Report
The impact report is brimming with achievements that underscore our progress, including:
- Global Registry Network Expansion – We have expanded our reach significantly, now covering 65 member registries across 41 countries, representing 88,832 individuals with neuromuscular diseases, including 51,352 with a genetic diagnosis.
- Educational Initiatives – We have translated essential resources like the Duchenne muscular dystrophy Family Care Guides and Spinal Muscular Atrophy International Standards of Care into multiple languages, ensuring accessibility worldwide. Additionally, our masterclass events and conferences have empowered hundreds of healthcare professionals globally.
- Advancing Therapeutics – TREAT-NMD is actively supporting nine drug development programs across five disease areas, providing critical advice and guidance to drive therapeutic innovation forward.
These achievements reflect not only the dedication of our team but also the collective efforts of our partners and supporters around the world.
Looking Ahead
As we reflect on the impact of our initiatives, we are energised by the possibilities ahead. With your continued support, TREAT-NMD will remain at the forefront of transforming the landscape of neuromuscular diseases, striving for a future where every individual affected receives the care and treatments they deserve.
We invite you to explore our full impact report below to learn more about the incredible progress made and the inspiring stories behind our journey.
Together, we are transforming lives.
