If you are a healthcare professional involved in the diagnosis of patients living with Duchenne muscular dystrophy (DMD), we invite you to express your interest in attending a virtual masterclass. The […]
TREAT-NMD News
Duchenne Muscular Dystrophy Early Diagnosis Project
The increasing prevalence of newborn genetic screening has led to earlier DMD diagnoses, with more and more patients being diagnosed prior to the development of symptoms. However, minimal clinical guidance […]
New AAN Evidence in Focus Article Highlights Gene Therapy for Duchenne Muscular Dystrophy
The American Academy of Neurology (AAN) has recently published a new Evidence in Focus article that may be of particular interest to the TREAT-NMD network. The piece, titled “Delandistrogene Moxeparvovec [...]
TREAT-NMD Announces Dr. Kathryn R. Wagner as New Chair of the Board
20 May 2025 – TREAT-NMD, a global network dedicated to accelerating treatments for neuromuscular diseases, is pleased to announce the appointment of Kathryn R. Wagner, MD, PhD, as its new […]
Project PaLaDIn
TREAT-NMD is the scientific coordinator of the IHI funded project PaLaDIn. The PaLaDIn consortium includes partners from SMEs, academia and patient advocacy organisations, working together to develop and implement a […]
We are pleased to announce the release of Version 1.0 of the TREAT-NMD Standard Neuromuscular Disease (sNMD) Dataset
The idea for the Standard Neuromuscular Disease (sNMD) dataset originated from the TREAT-NMD Ultra-Rare Subgroup (now known as the sNMD subgroup), led at the time by Robin Forbes (Australian Neuromuscular Disease Registry) […]
