We are pleased to announce that there is an open spot for a virtual TACT (TREAT-NMD Advisory Committee for Therapeutics) review on Tuesday, July 29th, 2025. This is a unique opportunity […]
News
Highlighting Cure HSPB8: Advocacy for a Rare Disease
HSPB8 Myopathy, also known as Myofibrillar Myopathy Type 13 with Rimmed Vacuoles (MFM13, OMIM: #621078) is an ultrarare, autosomal dominant muscle-wasting disease that typically begins in early adulthood. Despite its [...]
SMA White Paper updates to support SMA newborn screening
In SMA, newborn screening (NBS), dramatically change the life of young babies. SMA Europe has created an Alliance involving clinicians, patients, pharmaceutical industry and DNA testing producers, to promote SMA […]
2025 Annual Curators Meeting (ACM)
The 2025 Annual Curators Meeting (ACM) took place in Milan from February 10th to 12th, a fitting tribute to outgoing chair Anna Ambrosini, who calls the city home. This year’s […]
PaLaDIn General Assembly: A Milestone Event in Rome
On March 3rd and 4th, Rome will play host to the first General Assembly of the Patient Lifestyle and Disease Data Interactium (PaLaDIn) consortium. This highly anticipated event marks a […]
Upcoming Educational Masterclasses – Registrations Now Open!
TREAT-NMD® is proud to offer Expert-led Masterclasses providing high-quality, cutting-edge education for healthcare professionals involved in the diagnosis, management, and treatment of neuromuscular disorders. These immersive, in-person events are tailored […]
