TREAT-NMD is proud to participate in the upcoming 2025 MDA Clinical & Scientific Conference , an unparalleled gathering of global leaders dedicated to advancing neuromuscular disease research and care.
TREAT-NMD news
Project PaLaDIn Update
We have been working alongside other PaLaDIn partners to engage different groups, and most recently we held an industry engagement workshop alongside the TACT events in Boston. This brought together more than ten companies from across the neuromuscular disease space – from small biotechs to large pharmaceutical companies, those working at early and late stages, and those developing drugs in different diseases. The wish list identified by the group will be incorporated into the Interactium requirements as we start the system build next year.
Highlights from the TACT Symposium Developing Therapies for Rare Neuromuscular Diseases
The recent TACT Symposium, Developing Therapies in Rare Neuromuscular Diseases, which took place in Boston on the 31st of October, highlighted significant progress made in developing therapies over the past 15 years. Bringing together experts, researchers, clinicians, and stakeholders, the symposium focused on key milestones and lessons learned in improving patient outcomes.
BMD guidelines are now available in Italian, Spanish, English, Dutch, German and French
Working in collaboration with Parent Project – an association of patients and parents with children affected by Duchenne and Becker muscular dystrophy, TREAT-NMD has previously coordinated the translation of the guidelines into Spanish, and now into Dutch, German and French. Parent Project have also coordinated the translation of the document into English, thus making it available to an extremely wide international audience.
New Partnership Brings Hope for Duchenne Muscular Dystrophy
At TREAT-NMD, we are passionate about advancing the diagnosis, care and treatment for those living with neuromuscular disease and couldn’t be happier to hear about this new partnership between CureDuchenne and Blizzard Entertainment. The partnership aims to support the fight against Duchenne muscular dystrophy (DMD) through a unique in-game promotion in the popular game World of Warcraft®, helping to raise vital funds and awareness for DMD.
October is Charcot-Marie-Tooth (CMT) Awareness Month in the UK
This month, the spotlight is on Charcot-Marie-Tooth disease (CMT), a hereditary condition that affects the peripheral nerves, leading to muscle weakness and sensory changes, particularly in the hands and feet. Despite the complexity of this condition, the theme for this year, “Nobody Is Perfect”, emphasises that everyone is different, and regardless of how CMT affects someone, they can achieve great things.
